EventsCliniciansPacientsResearchersATMPsCell therapyGen TherapyBusiness ModelDrug DiscoveryEconomicsInvestmentMarketaccessRegulationResearchCTGCTGregor Cuzak 12 September 2024 Event Date: 6 September 2024 • 09:00 do: 6 September 2024 • European Commission Hosts Sixth Regional HTA Event in Budapest The European Commission recently held its sixth regional event in Budapest, focusing on the upcoming Health Technology Assessment (HTA) regulation. Set to launch in January 2025, this new framework aims to streamline the evaluation ... More
ArticlesPacientsResearchersCell therapyGen TherapyResearchCTGCTNICRodrigo Ortiz 30 August 2024 Exciting news in Sonogenetics: A New Frontier for Deep Tissue Treatment Researchers have made a discovery that could change how we treat some diseases deep within the human body. This technique, known as sonogenetics, combines the power of ultrasound with genetically engineered cells to deliver ... More
EventsResearchersCTGCTNICGregor Cuzak 12 August 2024 ADVANCE Workshop in June 2024 A diverse organising committee of various faculties from the University of Ljubljana organised a 5-day workshop called ADVANCE dedicated to translational medicine for advanced therapy medicinal products (ATMPs). Our Darja Marolt Presen participated. The ... More
EventsCliniciansResearchersGen TherapyDrug DiscoveryResearchCTGCTNICGregor Cuzak 17 July 2024 CTGCT about on/off switching of CAR-Ts at the EBMT 2024 Assoc. Prof Dr Mojca Benčina, head of the newly founded Slovenian Centre for the Technologies of Gene and Cell Therapy (CTGCT), gave a speech at the recent 50th Annual Meeting of the European Society ... More
CliniciansResearchersCell therapyGen TherapyGMPBusiness ModelClinic studyDrug DiscoveryEconomicsInvestmentLogisticsPre ClinicalResearchCTGCTNICUCLGregor Cuzak 17 July 2024 UCL ATMP Pipeline Our partner University College London (UCL) have produced a great short brochure (link) showing the strength and depth of their pipeline of ATMPs. They use a managed portfolio approach in which they support ~100 ... More
CliniciansPacientsResearchersBusiness ModelCharite BerlinCTGCTNICUCLUMCUtrechtGregor Cuzak 8 July 2024 The Promise and Price of Advanced Therapies Here’s what Claude Sonnet 3.5 has to answer when we question it: why do ATMPs cost so much? Advanced Therapy Medicinal Products (ATMPs), including gene and cell therapies, represent a revolutionary frontier in medicine, ... More
EventsCliniciansResearchersCell therapyGen TherapyGMPClinic studyMarketaccessRegulationResearchCharite BerlinCTGCTNICUMCUtrechtGregor Cuzak 1 July 2024 Panel Discussion on ATMP Regulation The CTGCT organised its first Panel Discussion on 29 May entitled: ATMP Regulation. The main takeaway from the very successful session was that the strong potential of the Slovenian ecosystem requires the will to ... More
InterviewResearchersDatamanagementDrug DiscoveryResearchCTGCTNICGregor Cuzak 27 June 2024 Interview with Shivang Khandewal – collaborator of NIC and CTNNB1 Originally from India, Shivang Khandelwal is presently engaged in advanced studies at the Hebrew University of Jerusalem. His primary research focus is on PCDH19 cluster epilepsy, a neurodevelopmental and neuropsychiatric disorder. He is deeply ... More
ArticlesCliniciansPacientsResearchersDrug DiscoveryMarketaccessRegulationResearchCTGCTGregor Cuzak 27 June 2024 Bespoke Gene Therapy Consortium – cooperation for rare disease therapies At the Bespoke Gene Therapy Consortium (BGTC, website), a consortium for the treatment of rare monogenetic diseases, they aim to treat neglected diseases with a very small number of patients with a focus solely ... More
EventsCliniciansPacientsResearchersGen TherapyGMPClinic studyDatamanagementDrug DiscoveryEthicalcommitteeInvestmentLaboratoryLogisticsManufacturing ProcessModalitetadelovanjazdravilaPharmacodynamicsPharmacokineticsPre ClinicalRaw MaterialRegulationResearchCTGCTNICGregor Cuzak 26 June 2024 Event Date: 14 June 2024 • 09:00 − 17:00 CTNNB1 Conference – One Year to Cure One year to cure is the goal shared by parents of children with the CTNNB1 Syndrome rare disease. Out of approximately 400 known cases worldwide, 82 families with children gathered at the conference in ... More
ArticlesResearchersDrug DiscoveryResearchNICMojca Bencina 20 June 2024 Protein Gas Vesicles – Potential to Improve Therapy, published in ACS Nano Ultrasound is a useful method in diagnostics, as it enables a deep and non-invasive observation of the body. Under certain conditions, ultrasound can stimulate cells, but this effect is very small and to amplify ... More
Events 28 May 2024 Event Date: 29 May 2024 • 11:00 − 12:30 CTGCT Panel Discussion #1: ATMP regulation The CTGCT Panel Discussion is a series of events of the Centre for Technology of Gene and Cell Therapies (CTGCT) aimed at addressing the prescient topics within the Advanced Therapies Medicinal Products (ATMP) field ... More