EventsResearchersCell therapyGen TherapyClinic studyMarketaccessRegulationCTGCTRodrigo Ortiz 5 November 2025 Event Date: 27 October 2025 do: 29 October 2025 • CTGCT Takeaways from the World Orphan Drug Congress Europe 2025 CTGCT attended the World Orphan Drug Congress (WODC) Europe 2025 in Amsterdam from the 27th to the 29th of October, an event dedicated to strategies and partnerships in the orphan drug industry. There were ... More
ATMPsCell therapyGen TherapyBusiness ModelDrug DiscoveryEconomicsMarketaccessRegulationCTGCTGregor Cuzak 10 October 2025 Academic developers for affordable medicines CTGCT (Centre for the Technologies of Gene and Cell Therapy, at National institute of Chemistry, Ljubljana) has joined the statement to preserve the Hospital Exemption in the revised EU pharmaceutical legislation. The Joint Statement, ... More
ArticlesCliniciansPacientsResearchersGen TherapyResearchCTGCTNICRodrigo Ortiz 25 September 2025 From Film Editing to RNA Editing: How RNA Trans-splicing Could Treat CTNNB1 Syndrome Imagine you're in a movie editing studio, trying to fix a film with some corrupted scenes. The film is vital, as it plays a crucial role in the development and function of an entire ... More
EventsCliniciansPacientsResearchersATMPsCell therapyGen TherapyResearchCharite BerlinCTGCTNICTUDUCLUMCUtrechtRodrigo Ortiz 4 July 2025 Event Date: 15 September 2025 do: 17 September 2025 • CTGCT Days 2025 – 15th to 17th September, Ljubljana REGISTER to join us at CTGCT Days 2025! A 3-day event in Ljubljana, Slovenia, spotlighting breakthroughs in gene & cell therapies (GCT) and their clinical translation. More
ArticlesCliniciansPacientsResearchersGen TherapyResearchRodrigo Ortiz 5 June 2025 Unraveling the Mysteries of NLRP3: A Key Player in Inflammation In the complex world of cellular biology, proteins play a crucial role in maintaining our body's health and responding to threats. One such protein, NLRP3, is known for its ability to assemble the inflammasome ... More
ArticlesCliniciansPacientsResearchersCell therapyGen TherapyLaboratoryResearchCTGCTNICRodrigo Ortiz 3 June 2025 Harnessing Synthetic Biology for Innovative Medical Treatments In the world of synthetic biology, scientists are pushing the boundaries of what's possible by designing proteins that can be controlled in specific ways. This review written by Tjaša Plaper, Urška Knez Štibler and ... More
EventsCliniciansPacientsResearchersATMPsCell therapyGen TherapyBusiness ModelMarketaccessCTGCTNICGregor Cuzak 20 May 2025 Event Date: 1 May 2025 do: 31 May 2025 • Posters at Krakovski nasip – Ljubljanica embankment In May 2025, our Centre for the Technologies of Gene and Cell Therapy CTGCT) is participating in a poster exhibition on Krakovski nasip, as part of the Chemical Institute’s public presentation. More
ArticlesEventsCliniciansPacientsResearchersGen TherapyRaziskaveCTGCTNICRodrigo Ortiz 8 April 2025 Event Date: 21 March 2025 do: 21 March 2025 • CTGCT’s Role in the GeneH Project: Accelerating Gene Therapy Innovations We are thrilled to announce our participation in the GeneH consortium, an ambitious project led by the University of Coimbra, and their GeneT project, colead by the Kemijski Inštitut with the CTGCT project, aimed ... More
EventsCliniciansResearchersGen TherapyResearchCTGCTRodrigo Ortiz 12 March 2025 Event Date: 17 March 2025 • 14:00 do: 17 March 2025 • 15:00 Gene Therapy: Triumphs, Challenges, and Future Directions Lecture by Luis Pereira de Almeida on the 17th of March at the Kemijski Inštitut More
ArticlesCliniciansResearchersATMPsCell therapyGen TherapyManufacturing ProcessRegulationCTGCTUMCUtrechtRodrigo Ortiz 5 March 2025 Navigating Viral Vector Production for Gene Therapy This week we had the opportunity to listen to Ganesh Ramesh, a PhD candidate at the Viral Vector Production Center for Translation Immunology of UMC Utrecht, under the supervision of Dr. Zsolt Sebestyen. Here ... More
ArticlesPacientsATMPsCell therapyGen TherapyBusiness ModelEconomicsPre ClinicalResearchCTGCTNICRodrigo Ortiz 28 February 2025 How Patient Advocacy is Driving Breakthroughs to Treat CTNNB1 Syndrome Imagine a world where a child’s genetic disorder, once considered untreatable, is finally on a path toward real solutions. For families affected by the CTNNB1 syndrome, that future is becoming a reality thanks to ... More
ArticlesPacientsResearchersGen TherapyLaboratoryPre ClinicalResearchCTGCTNICRodrigo Ortiz 28 January 2025 The research on combining cytokines with pyroptosis is gaining widespread media coverage Research on combining cytokines and pyroptosis for cancer therapy by Slovenian scientists has gained significant media recognition, including TV features, articles, and the honor of being named "Names of the Week". More